Genome editing in induced pluripotent stem cells rescues TAF1 levels in X-linked dystonia-parkinsonism
Rakovic A, Domingo A, Grütz K, Kulikovskaja L, Capetian P, Cowley SA, Lenz I, Brüggemann N, Rosales R, Jamora D4, Rolfs A, Seibler P, Westenberger A, König I, Klein C.
Mov Disord. 2018 Jul;33(7):1108-1118. doi: 10.1002/mds.27441.
https://www.ncbi.nlm.nih.gov/pubmed/30153385